1상모집 중
A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort
연구 개요
Cohort 8 (non-ambulatory participants) is currently enrolling new participants. Enrollment for Cohorts 1 through 7 has been completed. This is an open-label gene transfer therapy study evaluating the safety of and expression from delandistrogene moxeparvovec in participants with Duchenne Muscular Dystrophy (DMD). The maximum participant duration for this study is 156 weeks.
- 스폰서
- 협력: 로슈
- 적응증
- Duchenne Muscular Dystrophy
- 중재
- delandistrogene moxeparvovec
- 목표 등록
- 83명
- 시작일
- 2020-11-23
- 완료(예정)
- 2028-02-29
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